The world’s most expensive drug, Zolgensma, is a new £1.79m gene therapy used to treat muscular dystrophy.
The drug gave a baby in Britain a chance to live again after receiving the most expensive medical drug in the world.
baby Edward, one year old, of Colchester, Essex; He had spinal muscular atrophy; Which means it lacks a protein vital for muscle growth.
The National Health Service in Britain has made available the drug “Zolgensma”, a new gene therapy at a cost of 1.79 million pounds; to give it to Edward in August.
His mother, Megan Willis, said her child has since experienced positive mutations in his condition that she would not have imagined possible.
She added that he was now able to roll over and sit without help, and began to take his first steps with the help of those around him; According to “BBC”.
She continued, “The most I wished was that he could sit down, and I knew then that he would have a wonderful life.”
“We’ve been concentrating with him for a few weeks on walking, and he’s starting to move his legs on his own using custom shoes, which is an amazing feat,” she added.
And about her feelings, Willis said: “My eyes shed tears as I witnessed it for the first time… It was a wonderful moment.”
Learn about the most expensive medicine in the world and the disease it treats
Sabq electronic newspaper
already
2022-01-01
The world’s most expensive drug, Zolgensma, is a new £1.79m gene therapy used to treat muscular dystrophy.
The drug gave a baby in Britain a chance to live again after receiving the most expensive medical drug in the world.
baby Edward, one year old, of Colchester, Essex; He had spinal muscular atrophy; Which means it lacks a protein vital for muscle growth.
The National Health Service in Britain has made available the drug “Zolgensma”, a new gene therapy at a cost of 1.79 million pounds; to give it to Edward in August.
His mother, Megan Willis, said her child has since experienced positive mutations in his condition that she would not have imagined possible.
She added that he was now able to roll over and sit without help, and began to take his first steps with the help of those around him; According to “BBC”.
She continued, “The most I wished was that he could sit down, and I knew then that he would have a wonderful life.”
“We’ve been concentrating with him for a few weeks on walking, and he’s starting to move his legs on his own using custom shoes, which is an amazing feat,” she added.
And about her feelings, Willis said: “My eyes shed tears as I witnessed it for the first time… It was a wonderful moment.”
01 Jan 2022 – 28 Jumada I 1443
10:21 AM
The world’s most expensive drug, Zolgensma, is a new £1.79m gene therapy used to treat muscular dystrophy.
The drug gave a baby in Britain a chance to live again after receiving the most expensive medical drug in the world.
baby Edward, one year old, of Colchester, Essex; He had spinal muscular atrophy; Which means it lacks a protein vital for muscle growth.
The National Health Service in Britain has made available the drug “Zolgensma”, a new gene therapy at a cost of 1.79 million pounds; to give it to Edward in August.
His mother, Megan Willis, said her child has since experienced positive mutations in his condition that she would not have imagined possible.
She added that he was now able to roll over and sit without help, and began to take his first steps with the help of those around him; According to “BBC”.
She continued, “The most I wished was that he could sit down, and I knew then that he would have a wonderful life.”
“We’ve been concentrating with him for a few weeks on walking, and he’s starting to move his legs on his own using custom shoes, which is an amazing feat,” she added.
And about her feelings, Willis said: “My eyes shed tears as I witnessed it for the first time… It was a wonderful moment.”